JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
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1 Online-Ressource.
- Sprache
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Englisch
- Erschienen in
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JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam ; day:11 ; month:5 ; year:2024 ; pages:1-14
Journal of neurology ; (11.5.2024), 1-14
- Urheber
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Chiriboga, Claudia A.
Bruno, Claudio
Duong, Tina
Fischer, Dirk
Mercuri, Eugenio
Kirschner, Janbernd
Kostera-Pruszczyk, Anna
Jaber, Birgit
Gorni, Ksenija
Kletzl, Heidemarie
Carruthers, Imogen
Martin, Carmen
Scalco, Renata S.
Fontoura, Paulo
Muntoni, Francesco
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1007/s00415-024-12318-z
- URN
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urn:nbn:de:101:1-2407221025540.031058189330
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
14.08.2025, 10:47 MESZ
Datenpartner
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Beteiligte
- Chiriboga, Claudia A.
- Bruno, Claudio
- Duong, Tina
- Fischer, Dirk
- Mercuri, Eugenio
- Kirschner, Janbernd
- Kostera-Pruszczyk, Anna
- Jaber, Birgit
- Gorni, Ksenija
- Kletzl, Heidemarie
- Carruthers, Imogen
- Martin, Carmen
- Scalco, Renata S.
- Fontoura, Paulo
- Muntoni, Francesco
- SpringerLink (Online service)
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