Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
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Neuromuscular disorders. - 29, 11 (2019) , 842-856, ISSN: 1873-2364
- Ereignis
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Veröffentlichung
- (wo)
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Freiburg
- (wer)
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Universität
- (wann)
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2020
- Urheber
- DOI
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doi.org/10.1016/j.nmd.2019.09.007
- URN
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urn:nbn:de:bsz:25-freidok-1545907
- Rechteinformation
-
Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
10.06.2025, 00:08 MESZ
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Beteiligte
- De Vivo, Darryl C.
- Kirschner, Janbernd
- Farwell, Wildon
- Universität
Entstanden
- 2020
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