Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1750-1172
- Extent
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Online-Ressource
- Language
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Englisch
- Notes
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online resource.
- Bibliographic citation
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Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study ; volume:15 ; number:1 ; day:29 ; month:7 ; year:2020 ; pages:1-9 ; date:12.2020
Orphanet journal of rare diseases ; 15, Heft 1 (29.7.2020), 1-9, 12.2020
- Creator
- Contributor
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SpringerLink (Online service)
- DOI
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10.1186/s13023-020-01477-7
- URN
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urn:nbn:de:101:1-2020092522191179789140
- Rights
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
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14.08.2025, 10:50 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Kiefer, Petra
- Kirschner, Janbernd
- Pechmann, Astrid
- Langer, Thorsten
- SpringerLink (Online service)
Other Objects (12)
Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
Nusinersen - praktische Aspekte der Therapie bei Spinaler Muskelatrophie im klinischen Allltag
Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of the NURTURE study
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Advances in treatment of spinal muscular atrophy – new phenotypes, new challenges, new implications for care
Correction to: Risdiplam inpatients previously treated with other therapies for spinal muscular atrophy: an interim analysis from the JEWELFISH study
Die Hospizbewegung in Deutschland am Beispiel Recklinghausen
Diagnostik und Therapie der Spinalen Muskelatrophie
Untersuchung von altersabhängigen Veränderungen der paraspinalen Muskulatur mit monoklonalen Antikörpern gegen Myosin-heavy-chain Muskelfaserstrukturproteine mittels Immunfluoreszenz
Cathepsin D as biomarker in CSF of nusinersen‐treated patients with spinal muscular atrophy
Diagnosis and management of spinal muscular atrophy: part 1: recommendations for diagnosis, rehabilitation, orthopedic and nutritional care
Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
Nusinersen - praktische Aspekte der Therapie bei Spinaler Muskelatrophie im klinischen Allltag
Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of the NURTURE study
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Advances in treatment of spinal muscular atrophy – new phenotypes, new challenges, new implications for care
Correction to: Risdiplam inpatients previously treated with other therapies for spinal muscular atrophy: an interim analysis from the JEWELFISH study
Die Hospizbewegung in Deutschland am Beispiel Recklinghausen
Diagnostik und Therapie der Spinalen Muskelatrophie
Untersuchung von altersabhängigen Veränderungen der paraspinalen Muskulatur mit monoklonalen Antikörpern gegen Myosin-heavy-chain Muskelfaserstrukturproteine mittels Immunfluoreszenz
Cathepsin D as biomarker in CSF of nusinersen‐treated patients with spinal muscular atrophy
Diagnosis and management of spinal muscular atrophy: part 1: recommendations for diagnosis, rehabilitation, orthopedic and nutritional care
Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
Nusinersen - praktische Aspekte der Therapie bei Spinaler Muskelatrophie im klinischen Allltag
Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of the NURTURE study
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Advances in treatment of spinal muscular atrophy – new phenotypes, new challenges, new implications for care
Correction to: Risdiplam inpatients previously treated with other therapies for spinal muscular atrophy: an interim analysis from the JEWELFISH study
Die Hospizbewegung in Deutschland am Beispiel Recklinghausen
Diagnostik und Therapie der Spinalen Muskelatrophie
Untersuchung von altersabhängigen Veränderungen der paraspinalen Muskulatur mit monoklonalen Antikörpern gegen Myosin-heavy-chain Muskelfaserstrukturproteine mittels Immunfluoreszenz
Cathepsin D as biomarker in CSF of nusinersen‐treated patients with spinal muscular atrophy