Paula Rio
Biologin
Hat mitgewirkt an:
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Therapeutic gene editing in CD 34 + hematopoietic progenitors from Fanconi anemia patients
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Targeted gene therapy and cell reprogramming in F anconi anemia
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Adenine base editing efficiently restores the function of Fanconi anemia hematopoietic stem and progenitor cells
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Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia