Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia
- Standort
-
Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
-
Online-Ressource
- Sprache
-
Englisch
- Anmerkungen
-
JCI insight. - 9, 10 (2024) , e171650, ISSN: 2379-3708
- Ereignis
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Veröffentlichung
- (wo)
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Freiburg
- (wer)
-
Universität
- (wann)
-
2024
- Urheber
-
Giménez, Yari
Palacios, Manuel
Sánchez-Dominguez, Rebeca
Zorbas, Christiane
Peral, Jorge
Puzik, Alexander
Ugalde, Laura
Alberquilla, Omaira
Villanueva, Mariela
Rio, Paula
Galvez, Eva María
Da Costa, Lydie
Strullu, Marion
Catala, Albert
Ruiz-Llobet, Anna
Segovia, Jose Carlos
Sevilla, Julian
Strahm, Brigitte
Niemeyer, Charlotte
Beléndez, Cristina
Leblanc, Thierry M.
Lafontaine, Denis L.J
Bueren, Juan A.
Navarro, Susana
- DOI
-
10.1172/jci.insight.171650
- URN
-
urn:nbn:de:bsz:25-freidok-2491569
- Rechteinformation
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
14.08.2025, 11:00 MESZ
Datenpartner
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Beteiligte
- Giménez, Yari
- Palacios, Manuel
- Sánchez-Dominguez, Rebeca
- Zorbas, Christiane
- Peral, Jorge
- Puzik, Alexander
- Ugalde, Laura
- Alberquilla, Omaira
- Villanueva, Mariela
- Rio, Paula
- Galvez, Eva María
- Da Costa, Lydie
- Strullu, Marion
- Catala, Albert
- Ruiz-Llobet, Anna
- Segovia, Jose Carlos
- Sevilla, Julian
- Strahm, Brigitte
- Niemeyer, Charlotte
- Beléndez, Cristina
- Leblanc, Thierry M.
- Lafontaine, Denis L.J
- Bueren, Juan A.
- Navarro, Susana
- Universität
Entstanden
- 2024
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