Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia
- Location
-
Deutsche Nationalbibliothek Frankfurt am Main
- Extent
-
Online-Ressource
- Language
-
Englisch
- Notes
-
JCI insight. - 9, 10 (2024) , e171650, ISSN: 2379-3708
- Event
-
Veröffentlichung
- (where)
-
Freiburg
- (who)
-
Universität
- (when)
-
2024
- Creator
-
Giménez, Yari
Palacios, Manuel
Sánchez-Dominguez, Rebeca
Zorbas, Christiane
Peral, Jorge
Puzik, Alexander
Ugalde, Laura
Alberquilla, Omaira
Villanueva, Mariela
Rio, Paula
Galvez, Eva María
Da Costa, Lydie
Strullu, Marion
Catala, Albert
Ruiz-Llobet, Anna
Segovia, Jose Carlos
Sevilla, Julian
Strahm, Brigitte
Niemeyer, Charlotte
Beléndez, Cristina
Leblanc, Thierry M.
Lafontaine, Denis L.J
Bueren, Juan A.
Navarro, Susana
- DOI
-
10.1172/jci.insight.171650
- URN
-
urn:nbn:de:bsz:25-freidok-2491569
- Rights
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
-
14.08.2025, 11:00 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Giménez, Yari
- Palacios, Manuel
- Sánchez-Dominguez, Rebeca
- Zorbas, Christiane
- Peral, Jorge
- Puzik, Alexander
- Ugalde, Laura
- Alberquilla, Omaira
- Villanueva, Mariela
- Rio, Paula
- Galvez, Eva María
- Da Costa, Lydie
- Strullu, Marion
- Catala, Albert
- Ruiz-Llobet, Anna
- Segovia, Jose Carlos
- Sevilla, Julian
- Strahm, Brigitte
- Niemeyer, Charlotte
- Beléndez, Cristina
- Leblanc, Thierry M.
- Lafontaine, Denis L.J
- Bueren, Juan A.
- Navarro, Susana
- Universität
Time of origin
- 2024
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