Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
- Location
-
Deutsche Nationalbibliothek Frankfurt am Main
- Extent
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Online-Ressource
- Language
-
Englisch
- Notes
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Neuromuscular disorders. - 29, 11 (2019) , 842-856, ISSN: 1873-2364
- Event
-
Veröffentlichung
- (where)
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Freiburg
- (who)
-
Universität
- (when)
-
2020
- Creator
- DOI
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doi.org/10.1016/j.nmd.2019.09.007
- URN
-
urn:nbn:de:bsz:25-freidok-1545907
- Rights
-
Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
-
14.08.2025, 10:58 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- De Vivo, Darryl C.
- Kirschner, Janbernd
- Farwell, Wildon
- Universität
Time of origin
- 2020
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Die Hospizbewegung in Deutschland am Beispiel Recklinghausen
Diagnostik und Therapie der Spinalen Muskelatrophie
Untersuchung von altersabhängigen Veränderungen der paraspinalen Muskulatur mit monoklonalen Antikörpern gegen Myosin-heavy-chain Muskelfaserstrukturproteine mittels Immunfluoreszenz
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Correction to: Risdiplam inpatients previously treated with other therapies for spinal muscular atrophy: an interim analysis from the JEWELFISH study
Advances in treatment of spinal muscular atrophy – new phenotypes, new challenges, new implications for care
A checklist for clinical trials in rare disease: obstacles and anticipatory actions-lessons learned from the FOR-DMD trial
The TREAT‐NMD DMD global database: analysis of more than 7,000 duchenne muscular dystrophy mutations
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of the NURTURE study
Nusinersen - praktische Aspekte der Therapie bei Spinaler Muskelatrophie im klinischen Allltag
Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study
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Diagnostik und Therapie der Spinalen Muskelatrophie
Untersuchung von altersabhängigen Veränderungen der paraspinalen Muskulatur mit monoklonalen Antikörpern gegen Myosin-heavy-chain Muskelfaserstrukturproteine mittels Immunfluoreszenz
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Correction to: Risdiplam inpatients previously treated with other therapies for spinal muscular atrophy: an interim analysis from the JEWELFISH study
Advances in treatment of spinal muscular atrophy – new phenotypes, new challenges, new implications for care
A checklist for clinical trials in rare disease: obstacles and anticipatory actions-lessons learned from the FOR-DMD trial