Survival and associated factors in 268 adults with Pompe disease prior to treatment with enzyme replacement therapy
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1750-1172
- Extent
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Online-Ressource
- Language
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Englisch
- Notes
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online resource.
- Bibliographic citation
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Survival and associated factors in 268 adults with Pompe disease prior to treatment with enzyme replacement therapy ; volume:6 ; number:1 ; day:1 ; month:6 ; year:2011 ; pages:1-8 ; date:12.2011
Orphanet journal of rare diseases ; 6, Heft 1 (1.6.2011), 1-8, 12.2011
- Creator
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Güngör, Deniz
- Contributor
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de Vries, Juna M.
Hop, Wim CJ
Reuser, Arnold JJ
van Doorn, Pieter A.
van der Ploeg, Ans T.
Hagemans, Marloes LC
SpringerLink (Online service)
- DOI
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10.1186/1750-1172-6-34
- URN
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urn:nbn:de:1111-2016050120073
- Rights
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Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
-
14.08.2025, 10:44 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Güngör, Deniz
- de Vries, Juna M.
- Hop, Wim CJ
- Reuser, Arnold JJ
- van Doorn, Pieter A.
- van der Ploeg, Ans T.
- Hagemans, Marloes LC
- SpringerLink (Online service)
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Improved Enzyme Replacement Therapy with Cipaglucosidase Alfa/Miglustat in Infantile Pompe Disease
Impact of enzyme replacement therapy on survival in adults with Pompe disease
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in adult patients with Pompe disease
Long-term follow-up of 17 patients with childhood Pompe disease treated with enzyme replacement therapy
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease
Improvement of dysphagia in a child affected by Pompe disease treated with enzyme replacement therapy
Home-based enzyme replacement therapy in children and adults with Pompe disease; a prospective study
Correction of oxidative stress enhances enzyme replacement therapy in Pompe disease
The impact of interrupting enzyme replacement therapy in late-onset Pompe disease
Hearing characteristics of infantile-onset Pompe disease after early enzyme-replacement therapy
Enzyme replacement therapy and fatigue in adults with Pompe disease
Enzyme replacement therapy (ERT) in pompe disease
Improved Enzyme Replacement Therapy with Cipaglucosidase Alfa/Miglustat in Infantile Pompe Disease
Impact of enzyme replacement therapy on survival in adults with Pompe disease
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in adult patients with Pompe disease
Long-term follow-up of 17 patients with childhood Pompe disease treated with enzyme replacement therapy
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease
Improvement of dysphagia in a child affected by Pompe disease treated with enzyme replacement therapy
Home-based enzyme replacement therapy in children and adults with Pompe disease; a prospective study
Correction of oxidative stress enhances enzyme replacement therapy in Pompe disease
The impact of interrupting enzyme replacement therapy in late-onset Pompe disease