Home-based enzyme replacement therapy in children and adults with Pompe disease; a prospective study
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
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Online-Ressource, 1 online resource.
- Sprache
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Englisch
- Erschienen in
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Home-based enzyme replacement therapy in children and adults with Pompe disease; a prospective study ; volume:18 ; number:1 ; day:8 ; month:5 ; year:2023 ; pages:1-10 ; date:12.2023
Orphanet journal of rare diseases ; 18, Heft 1 (8.5.2023), 1-10, 12.2023
- Urheber
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Ditters, Imke A. M.
van der Beek, Nadine A. M. E.
Brusse, Esther
van der Ploeg, Ans T.
van den Hout, Johanna M. P.
Huidekoper, Hidde H.
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1186/s13023-023-02715-4
- URN
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urn:nbn:de:101:1-2023090708233385631514
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
14.08.2025, 10:58 MESZ
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Beteiligte
- Ditters, Imke A. M.
- van der Beek, Nadine A. M. E.
- Brusse, Esther
- van der Ploeg, Ans T.
- van den Hout, Johanna M. P.
- Huidekoper, Hidde H.
- SpringerLink (Online service)
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