N-acetyl-L-leucine for Niemann-Pick type C: a multinational double-blind randomized placebo-controlled crossover study
- Standort
-
Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
-
Online-Ressource, 1 online resource.
- Sprache
-
Englisch
- Erschienen in
-
N-acetyl-L-leucine for Niemann-Pick type C: a multinational double-blind randomized placebo-controlled crossover study ; volume:24 ; number:1 ; day:29 ; month:5 ; year:2023 ; pages:1-9 ; date:12.2023
Trials ; 24, Heft 1 (29.5.2023), 1-9, 12.2023
- Urheber
-
Fields, T.
M. Bremova, T.
Billington, I.
Churchill, GC
Evans, W.
Fields, C.
Galione, A.
Kay, R.
Mathieson, T.
Martakis, K.
Patterson, M.
Platt, F.
Factor, M.
Strupp, M.
- Beteiligte Personen und Organisationen
-
SpringerLink (Online service)
- DOI
-
10.1186/s13063-023-07399-6
- URN
-
urn:nbn:de:101:1-2023091109460845226285
- Rechteinformation
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
14.08.2025, 11:03 MESZ
Datenpartner
Dieses Objekt wird bereitgestellt von:
Deutsche Nationalbibliothek. Bei Fragen zum Objekt wenden Sie sich bitte an den Datenpartner.
Deutsche Nationalbibliothek. Bei Fragen zum Objekt wenden Sie sich bitte an den Datenpartner.
Beteiligte
- Fields, T.
- M. Bremova, T.
- Billington, I.
- Churchill, GC
- Evans, W.
- Fields, C.
- Galione, A.
- Kay, R.
- Mathieson, T.
- Martakis, K.
- Patterson, M.
- Platt, F.
- Factor, M.
- Strupp, M.
- SpringerLink (Online service)
Ähnliche Objekte (12)
Efficacy and safety of N-acetyl-l-leucine in Niemann–Pick disease type C
Niemann-Pick type C disease: effects of a therapy with acetyl-DL-leucine and vestibular function
Effects of acetyl-DL-leucine on cerebellar ataxia (ALCAT trial): study protocol for a multicenter, multinational, randomized, double-blind, placebo-controlled, crossover phase III trial
A master protocol to investigate a novel therapy acetyl-l-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia
Acetyl-DL-leucine improves gait variability in patients with cerebellar ataxia—a case series
Morbus Niemann-Pick
Niemann-Pick disease
Niemann-Pick disease type C
Acetyl-DL-leucine in combination with memantine improves acquired pendular nystagmus caused by multiple sclerosis: a case report
Acetyl-dl-leucine in cerebellar ataxia ([18F]-FDG-PET study): how does a cerebellar disorder influence cortical sensorimotor networks?
Treatment trials in Niemann-Pick type C disease
Clinical disease characteristics of patients with Niemann-Pick Disease Type C: findings from the International Niemann-Pick Disease Registry (INPDR)
Efficacy and safety of N-acetyl-l-leucine in Niemann–Pick disease type C
Niemann-Pick type C disease: effects of a therapy with acetyl-DL-leucine and vestibular function
Effects of acetyl-DL-leucine on cerebellar ataxia (ALCAT trial): study protocol for a multicenter, multinational, randomized, double-blind, placebo-controlled, crossover phase III trial
A master protocol to investigate a novel therapy acetyl-l-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia
Acetyl-DL-leucine improves gait variability in patients with cerebellar ataxia—a case series
Morbus Niemann-Pick
Niemann-Pick disease
Niemann-Pick disease type C
Acetyl-DL-leucine in combination with memantine improves acquired pendular nystagmus caused by multiple sclerosis: a case report
Acetyl-dl-leucine in cerebellar ataxia ([18F]-FDG-PET study): how does a cerebellar disorder influence cortical sensorimotor networks?
Treatment trials in Niemann-Pick type C disease
Clinical disease characteristics of patients with Niemann-Pick Disease Type C: findings from the International Niemann-Pick Disease Registry (INPDR)
Efficacy and safety of N-acetyl-l-leucine in Niemann–Pick disease type C
Niemann-Pick type C disease: effects of a therapy with acetyl-DL-leucine and vestibular function
Effects of acetyl-DL-leucine on cerebellar ataxia (ALCAT trial): study protocol for a multicenter, multinational, randomized, double-blind, placebo-controlled, crossover phase III trial
A master protocol to investigate a novel therapy acetyl-l-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia
Acetyl-DL-leucine improves gait variability in patients with cerebellar ataxia—a case series
Morbus Niemann-Pick
Niemann-Pick disease
Niemann-Pick disease type C
Acetyl-DL-leucine in combination with memantine improves acquired pendular nystagmus caused by multiple sclerosis: a case report
Acetyl-dl-leucine in cerebellar ataxia ([18F]-FDG-PET study): how does a cerebellar disorder influence cortical sensorimotor networks?
Treatment trials in Niemann-Pick type C disease