A master protocol to investigate a novel therapy acetyl-l-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia

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Location: Deutsche Nationalbibliothek Frankfurt am Main

ISSN: 1745-6215

Extent: Online-Ressource

Language: Englisch

Notes: online resource.

Bibliographic citation: A master protocol to investigate a novel therapy acetyl-l-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia ; volume:22 ; number:1 ; day:22 ; month:1 ; year:2021 ; pages:1-15 ; date:12.2021
Trials ; 22, Heft 1 (22.1.2021), 1-15, 12.2021

Creator: Fields, T.
Patterson, M.
Bremova-Ertl, T.
Belcher, G.
Billington, I.
Churchill, G. C.
Davis, W.
Evans, W.
Flint, S.
Galione, A.
Granzer, U.
Greenfield, J.
Karl, R.
Kay, R.
Lewi, D.
Mathieson, T.
Meyer, T.
Pangonis, D.
Platt, F. M.
Tsang, L.
Verburg, C.
Factor, M.
Strupp, M.

Contributor: SpringerLink (Online service)

DOI: 10.1186/s13063-020-05009-3

URN: urn:nbn:de:101:1-2021031420280109191131

Rights: Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.

Last update: 15.08.2025, 7:31 AM CEST

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Associated

Fields, T.
Patterson, M.
Bremova-Ertl, T.
Belcher, G.
Billington, I.
Churchill, G. C.
Davis, W.
Evans, W.
Flint, S.
Galione, A.
Granzer, U.
Greenfield, J.
Karl, R.
Kay, R.
Lewi, D.
Mathieson, T.
Meyer, T.
Pangonis, D.
Platt, F. M.
Tsang, L.
Verburg, C.
Factor, M.
Strupp, M.
SpringerLink (Online service)

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A master protocol to investigate a novel therapy acetyl-l-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia

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Other Objects (12)

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