The role of ataluren in the treatment of ambulatory and non-ambulatory children with nonsense mutation duchenne muscular dystrophy - a consensus derived using a modified Delphi methodology in Eastern Europe, Greece, Israel and Sweden
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- Extent
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1 Online-Ressource.
- Language
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Englisch
- Bibliographic citation
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The role of ataluren in the treatment of ambulatory and non-ambulatory children with nonsense mutation duchenne muscular dystrophy - a consensus derived using a modified Delphi methodology in Eastern Europe, Greece, Israel and Sweden ; volume:24 ; number:1 ; day:21 ; month:2 ; year:2024 ; pages:1-9 ; date:12.2024
BMC neurology ; 24, Heft 1 (21.2.2024), 1-9, 12.2024
- Classification
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Biowissenschaften, Biologie
- Creator
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Golli, Tanja
Juříková, Lenka
Sejersen, Thomas
Dixon, Craig
- Contributor
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SpringerLink (Online service)
- DOI
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10.1186/s12883-024-03570-x
- URN
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urn:nbn:de:101:1-2404291400459.886720038231
- Rights
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
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14.08.2025, 10:49 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Golli, Tanja
- Juříková, Lenka
- Sejersen, Thomas
- Dixon, Craig
- SpringerLink (Online service)
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Characteristics of disease progression and genetic correlation in ambulatory Iranian boys with Duchenne muscular dystrophy
Symptoms and impacts of ambulatory nonsense mutation Duchenne muscular dystrophy: a qualitative study and the development of a patient-centred conceptual model
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Lower extremity joint contracture according to ambulatory status in children with Duchenne muscular dystrophy
Characteristics of disease progression and genetic correlation in ambulatory Iranian boys with Duchenne muscular dystrophy
Symptoms and impacts of ambulatory nonsense mutation Duchenne muscular dystrophy: a qualitative study and the development of a patient-centred conceptual model
Exploring the relationship between North Star Ambulatory Assessment and Health Utilities Index scores in Duchenne muscular dystrophy
Survival in Duchenne muscular dystrophy
Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
Targeting angiogenesis in Duchenne muscular dystrophy
Pain characterization in Duchenne muscular dystrophy
Cognition trajectory in Duchenne muscular dystrophy
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A qualitative study on the impact of caring for an ambulatory individual with nonsense mutation Duchenne muscular dystrophy
Safety and efficacy of viltolarsen in ambulatory and nonambulatory males with Duchenne muscular dystrophy
Lower extremity joint contracture according to ambulatory status in children with Duchenne muscular dystrophy
Characteristics of disease progression and genetic correlation in ambulatory Iranian boys with Duchenne muscular dystrophy
Symptoms and impacts of ambulatory nonsense mutation Duchenne muscular dystrophy: a qualitative study and the development of a patient-centred conceptual model
Exploring the relationship between North Star Ambulatory Assessment and Health Utilities Index scores in Duchenne muscular dystrophy
Survival in Duchenne muscular dystrophy
Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
Targeting angiogenesis in Duchenne muscular dystrophy
Pain characterization in Duchenne muscular dystrophy
Cognition trajectory in Duchenne muscular dystrophy