The role of ataluren in the treatment of ambulatory and non-ambulatory children with nonsense mutation duchenne muscular dystrophy - a consensus derived using a modified Delphi methodology in Eastern Europe, Greece, Israel and Sweden
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
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1 Online-Ressource.
- Sprache
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Englisch
- Erschienen in
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The role of ataluren in the treatment of ambulatory and non-ambulatory children with nonsense mutation duchenne muscular dystrophy - a consensus derived using a modified Delphi methodology in Eastern Europe, Greece, Israel and Sweden ; volume:24 ; number:1 ; day:21 ; month:2 ; year:2024 ; pages:1-9 ; date:12.2024
BMC neurology ; 24, Heft 1 (21.2.2024), 1-9, 12.2024
- Klassifikation
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Biowissenschaften, Biologie
- Urheber
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Golli, Tanja
Juříková, Lenka
Sejersen, Thomas
Dixon, Craig
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1186/s12883-024-03570-x
- URN
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urn:nbn:de:101:1-2404291400459.886720038231
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
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14.08.2025, 10:49 MESZ
Datenpartner
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Beteiligte
- Golli, Tanja
- Juříková, Lenka
- Sejersen, Thomas
- Dixon, Craig
- SpringerLink (Online service)
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