Forced vital capacity and cross-domain late-onset Pompe disease outcomes: an individual patient-level data meta-analysis

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Location: Deutsche Nationalbibliothek Frankfurt am Main

ISSN: 1432-1459

Extent: Online-Ressource

Language: Englisch

Notes: online resource.

Bibliographic citation: Forced vital capacity and cross-domain late-onset Pompe disease outcomes: an individual patient-level data meta-analysis ; volume:266 ; number:9 ; day:11 ; month:6 ; year:2019 ; pages:2312-2321 ; date:9.2019
Journal of neurology ; 266, Heft 9 (11.6.2019), 2312-2321, 9.2019

Creator: Berger, Kenneth I.
Kanters, Steve
Jansen, Jeroen P.
Stewart, Andrew
Sparks, Susan
Haack, Kristina An
Bolzani, Anna
Siliman, Gaye
Hamed, Alaa

Contributor: SpringerLink (Online service)

DOI: 10.1007/s00415-019-09401-1

URN: urn:nbn:de:101:1-2019122906485146586206

Rights: Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.

Last update: 14.08.2025, 10:53 AM CEST

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Berger, Kenneth I.
Kanters, Steve
Jansen, Jeroen P.
Stewart, Andrew
Sparks, Susan
Haack, Kristina An
Bolzani, Anna
Siliman, Gaye
Hamed, Alaa
SpringerLink (Online service)

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Forced vital capacity and cross-domain late-onset Pompe disease outcomes: an individual patient-level data meta-analysis

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Other Objects (12)

Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry

Fatigue: an important feature of late-onset Pompe disease

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Bright tongue sign in patients with late-onset Pompe disease

Walking delay as leading symptom in late-onset Pompe disease

Alglucosidase alfa: 5 years of experience in late-onset Pompe disease

Analysis of voice quality in patients with late-onset Pompe disease

Abnormal tongue features as a clinical clue for late-onset Pompe's disease

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The impact of interrupting enzyme replacement therapy in late-onset Pompe disease

Screening for late-onset Pompe disease in Internal Medicine departments in Spain

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Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry

Fatigue: an important feature of late-onset Pompe disease

Late-Onset Pompe Disease Presenting with Isolated Tongue Involvement

Bright tongue sign in patients with late-onset Pompe disease

Walking delay as leading symptom in late-onset Pompe disease

Alglucosidase alfa: 5 years of experience in late-onset Pompe disease

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Fatigue: an important feature of late-onset Pompe disease

Late-Onset Pompe Disease Presenting with Isolated Tongue Involvement

Bright tongue sign in patients with late-onset Pompe disease

Walking delay as leading symptom in late-onset Pompe disease

Alglucosidase alfa: 5 years of experience in late-onset Pompe disease

Analysis of voice quality in patients with late-onset Pompe disease

Abnormal tongue features as a clinical clue for late-onset Pompe's disease

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The impact of interrupting enzyme replacement therapy in late-onset Pompe disease

Screening for late-onset Pompe disease in Internal Medicine departments in Spain

Follow-up analysis of voice quality in patients with late-onset Pompe disease

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