Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry

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Location: Deutsche Nationalbibliothek Frankfurt am Main

Extent: 1 Online-Ressource.

Language: Englisch

Bibliographic citation: Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry ; volume:271 ; number:8 ; day:19 ; month:6 ; year:2024 ; pages:5433-5446 ; date:8.2024
Journal of neurology ; 271, Heft 8 (19.6.2024), 5433-5446, 8.2024

Creator: Berger, Kenneth I.
Chien, Yin-Hsiu
Dubrovsky, Alberto
Kishnani, Priya S.
Llerena, Juan C.
Neilan, Edward
Roberts, Mark
Sheng, Bun
Batista, Julie L.
Periquet, Magali
Wilson, Kathryn M.
Ploeg, Ans T. van der

Contributor: SpringerLink (Online service)

DOI: 10.1007/s00415-024-12489-9

URN: urn:nbn:de:101:1-2410310813512.682113227454

Rights: Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.

Last update: 15.08.2025, 7:23 AM CEST

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Berger, Kenneth I.
Chien, Yin-Hsiu
Dubrovsky, Alberto
Kishnani, Priya S.
Llerena, Juan C.
Neilan, Edward
Roberts, Mark
Sheng, Bun
Batista, Julie L.
Periquet, Magali
Wilson, Kathryn M.
Ploeg, Ans T. van der
SpringerLink (Online service)

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Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry

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