Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
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1 Online-Ressource.
- Sprache
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Englisch
- Erschienen in
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Changes in forced vital capacity over ≤ 13 years among patients with late-onset Pompe disease treated with alglucosidase alfa: new modeling of real-world data from the Pompe Registry ; volume:271 ; number:8 ; day:19 ; month:6 ; year:2024 ; pages:5433-5446 ; date:8.2024
Journal of neurology ; 271, Heft 8 (19.6.2024), 5433-5446, 8.2024
- Urheber
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Berger, Kenneth I.
Chien, Yin-Hsiu
Dubrovsky, Alberto
Kishnani, Priya S.
Llerena, Juan C.
Neilan, Edward
Roberts, Mark
Sheng, Bun
Batista, Julie L.
Periquet, Magali
Wilson, Kathryn M.
Ploeg, Ans T. van der
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1007/s00415-024-12489-9
- URN
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urn:nbn:de:101:1-2410310813512.682113227454
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
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15.08.2025, 07:23 MESZ
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Beteiligte
- Berger, Kenneth I.
- Chien, Yin-Hsiu
- Dubrovsky, Alberto
- Kishnani, Priya S.
- Llerena, Juan C.
- Neilan, Edward
- Roberts, Mark
- Sheng, Bun
- Batista, Julie L.
- Periquet, Magali
- Wilson, Kathryn M.
- Ploeg, Ans T. van der
- SpringerLink (Online service)
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