Dystrophin and mini-dystrophin quantification by mass spectrometry in skeletal muscle for gene therapy development in Duchenne muscular dystrophy
- Location
-
Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
-
1476-5462
- Extent
-
Online-Ressource
- Language
-
Englisch
- Notes
-
online resource.
- Bibliographic citation
-
Dystrophin and mini-dystrophin quantification by mass spectrometry in skeletal muscle for gene therapy development in Duchenne muscular dystrophy ; volume:29 ; number:10-11 ; day:5 ; month:11 ; year:2021 ; pages:608-615 ; date:11.2022
Gene therapy ; 29, Heft 10-11 (5.11.2021), 608-615, 11.2022
- Creator
-
Farrokhi, Vahid
Walsh, Jason
Palandra, Joe
Brodfuehrer, Joanne
Caiazzo, Teresa
Owens, Jane
Binks, Michael
Neelakantan, Srividya
Yong, Florence
Dua, Pinky
Guiner, Caroline Le
Neubert, Hendrik
- Contributor
-
SpringerLink (Online service)
- DOI
-
10.1038/s41434-021-00300-7
- URN
-
urn:nbn:de:101:1-2023020409133697217318
- Rights
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
-
14.08.2025, 10:59 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Farrokhi, Vahid
- Walsh, Jason
- Palandra, Joe
- Brodfuehrer, Joanne
- Caiazzo, Teresa
- Owens, Jane
- Binks, Michael
- Neelakantan, Srividya
- Yong, Florence
- Dua, Pinky
- Guiner, Caroline Le
- Neubert, Hendrik
- SpringerLink (Online service)
Other Objects (12)
Dystrophin Dp71 and the Neuropathophysiology of Duchenne Muscular Dystrophy
Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy
Systemic delivery of full-length dystrophin in Duchenne muscular dystrophy mice
Dystrophin Expressing Chimeric (DEC) Human Cells Provide a Potential Therapy for Duchenne Muscular Dystrophy
Deletion pattern in the dystrophin gene in Duchenne muscular dystrophy patients in northeast India
Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review
In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers
Cell transplantation-mediated dystrophin supplementation efficacy in Duchenne muscular dystrophy mouse motor function improvement demonstrated by enhanced skeletal muscle fatigue tolerance
Altered social behavior and ultrasonic communication in the dystrophin-deficient mdx mouse model of Duchenne muscular dystrophy
Prenatal diagnosis of Duchenne muscular dystrophy revealed a novel mosaic mutation in Dystrophin gene: a case report
Engraftment of human induced pluripotent stem cell-derived myogenic progenitors restores dystrophin in mice with duchenne muscular dystrophy
Timing and localization of human dystrophin isoform expression provide insights into the cognitive phenotype of Duchenne muscular dystrophy
Dystrophin Dp71 and the Neuropathophysiology of Duchenne Muscular Dystrophy
Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy
Systemic delivery of full-length dystrophin in Duchenne muscular dystrophy mice
Dystrophin Expressing Chimeric (DEC) Human Cells Provide a Potential Therapy for Duchenne Muscular Dystrophy
Deletion pattern in the dystrophin gene in Duchenne muscular dystrophy patients in northeast India
Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review
In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers
Cell transplantation-mediated dystrophin supplementation efficacy in Duchenne muscular dystrophy mouse motor function improvement demonstrated by enhanced skeletal muscle fatigue tolerance
Altered social behavior and ultrasonic communication in the dystrophin-deficient mdx mouse model of Duchenne muscular dystrophy
Prenatal diagnosis of Duchenne muscular dystrophy revealed a novel mosaic mutation in Dystrophin gene: a case report
Engraftment of human induced pluripotent stem cell-derived myogenic progenitors restores dystrophin in mice with duchenne muscular dystrophy
Timing and localization of human dystrophin isoform expression provide insights into the cognitive phenotype of Duchenne muscular dystrophy
Dystrophin Dp71 and the Neuropathophysiology of Duchenne Muscular Dystrophy
Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy
Systemic delivery of full-length dystrophin in Duchenne muscular dystrophy mice
Dystrophin Expressing Chimeric (DEC) Human Cells Provide a Potential Therapy for Duchenne Muscular Dystrophy
Deletion pattern in the dystrophin gene in Duchenne muscular dystrophy patients in northeast India
Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review
In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers
Cell transplantation-mediated dystrophin supplementation efficacy in Duchenne muscular dystrophy mouse motor function improvement demonstrated by enhanced skeletal muscle fatigue tolerance
Altered social behavior and ultrasonic communication in the dystrophin-deficient mdx mouse model of Duchenne muscular dystrophy
Prenatal diagnosis of Duchenne muscular dystrophy revealed a novel mosaic mutation in Dystrophin gene: a case report
Engraftment of human induced pluripotent stem cell-derived myogenic progenitors restores dystrophin in mice with duchenne muscular dystrophy