Dystrophin and mini-dystrophin quantification by mass spectrometry in skeletal muscle for gene therapy development in Duchenne muscular dystrophy
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1476-5462
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
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online resource.
- Erschienen in
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Dystrophin and mini-dystrophin quantification by mass spectrometry in skeletal muscle for gene therapy development in Duchenne muscular dystrophy ; volume:29 ; number:10-11 ; day:5 ; month:11 ; year:2021 ; pages:608-615 ; date:11.2022
Gene therapy ; 29, Heft 10-11 (5.11.2021), 608-615, 11.2022
- Urheber
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Farrokhi, Vahid
Walsh, Jason
Palandra, Joe
Brodfuehrer, Joanne
Caiazzo, Teresa
Owens, Jane
Binks, Michael
Neelakantan, Srividya
Yong, Florence
Dua, Pinky
Guiner, Caroline Le
Neubert, Hendrik
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1038/s41434-021-00300-7
- URN
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urn:nbn:de:101:1-2023020409133697217318
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
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14.08.2025, 10:59 MESZ
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Beteiligte
- Farrokhi, Vahid
- Walsh, Jason
- Palandra, Joe
- Brodfuehrer, Joanne
- Caiazzo, Teresa
- Owens, Jane
- Binks, Michael
- Neelakantan, Srividya
- Yong, Florence
- Dua, Pinky
- Guiner, Caroline Le
- Neubert, Hendrik
- SpringerLink (Online service)
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Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy
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