Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice

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Location
Deutsche Nationalbibliothek Frankfurt am Main
ISSN
2041-1723
Extent
Online-Ressource
Language
Englisch
Notes
online resource.

Bibliographic citation
Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice ; volume:13 ; number:1 ; day:7 ; month:6 ; year:2022 ; pages:1-13 ; date:12.2022
Nature Communications ; 13, Heft 1 (7.6.2022), 1-13, 12.2022

Creator
Pontoizeau, Clément
Simon-Sola, Marcelo
Gaborit, Clovis
Nguyen, Vincent
Rotaru, Irina
Tual, Nolan
Colella, Pasqualina
Girard, Muriel
Biferi, Maria-Grazia
Arnoux, Jean-Baptiste
Rötig, Agnès
Ottolenghi, Chris
Lonlay, Pascale de
Mingozzi, Federico
Cavazzana, Marina
Schiff, Manuel
Contributor
SpringerLink (Online service)

DOI
10.1038/s41467-022-30880-w
URN
urn:nbn:de:101:1-2022080422444969604238
Rights
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
Last update
2025-08-15T07:22:05+0200

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Associated

  • Pontoizeau, Clément
  • Simon-Sola, Marcelo
  • Gaborit, Clovis
  • Nguyen, Vincent
  • Rotaru, Irina
  • Tual, Nolan
  • Colella, Pasqualina
  • Girard, Muriel
  • Biferi, Maria-Grazia
  • Arnoux, Jean-Baptiste
  • Rötig, Agnès
  • Ottolenghi, Chris
  • Lonlay, Pascale de
  • Mingozzi, Federico
  • Cavazzana, Marina
  • Schiff, Manuel
  • SpringerLink (Online service)

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