Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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2041-1723
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
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online resource.
- Erschienen in
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Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice ; volume:13 ; number:1 ; day:7 ; month:6 ; year:2022 ; pages:1-13 ; date:12.2022
Nature Communications ; 13, Heft 1 (7.6.2022), 1-13, 12.2022
- Urheber
-
Pontoizeau, Clément
Simon-Sola, Marcelo
Gaborit, Clovis
Nguyen, Vincent
Rotaru, Irina
Tual, Nolan
Colella, Pasqualina
Girard, Muriel
Biferi, Maria-Grazia
Arnoux, Jean-Baptiste
Rötig, Agnès
Ottolenghi, Chris
Lonlay, Pascale de
Mingozzi, Federico
Cavazzana, Marina
Schiff, Manuel
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1038/s41467-022-30880-w
- URN
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urn:nbn:de:101:1-2022080422444969604238
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
15.08.2025, 07:22 MESZ
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Beteiligte
- Pontoizeau, Clément
- Simon-Sola, Marcelo
- Gaborit, Clovis
- Nguyen, Vincent
- Rotaru, Irina
- Tual, Nolan
- Colella, Pasqualina
- Girard, Muriel
- Biferi, Maria-Grazia
- Arnoux, Jean-Baptiste
- Rötig, Agnès
- Ottolenghi, Chris
- Lonlay, Pascale de
- Mingozzi, Federico
- Cavazzana, Marina
- Schiff, Manuel
- SpringerLink (Online service)
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