Minimal clinically important differences in six-minute walking distance in late-onset Pompe disease

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Location: Deutsche Nationalbibliothek Frankfurt am Main

Extent: 1 Online-Ressource.

Language: Englisch

Bibliographic citation: Minimal clinically important differences in six-minute walking distance in late-onset Pompe disease ; volume:19 ; number:1 ; day:11 ; month:4 ; year:2024 ; pages:1-10 ; date:12.2024
Orphanet journal of rare diseases ; 19, Heft 1 (11.4.2024), 1-10, 12.2024

Creator: Claeys, Kristl G.
Kushlaf, Hani
Raza, Syed
Hummel, Noemi
Shohet, Simon
Keyzor, Ian
Kopiec, Agnieszka
Graham, Ryan
Fox, Brian
Schoser, Benedikt

Contributor: SpringerLink (Online service)

DOI: 10.1186/s13023-024-03156-3

URN: urn:nbn:de:101:1-2406251029005.822856071180

Rights: Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.

Last update: 14.08.2025, 11:01 AM CEST

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Claeys, Kristl G.
Kushlaf, Hani
Raza, Syed
Hummel, Noemi
Shohet, Simon
Keyzor, Ian
Kopiec, Agnieszka
Graham, Ryan
Fox, Brian
Schoser, Benedikt
SpringerLink (Online service)

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Minimal clinically important differences in six-minute walking distance in late-onset Pompe disease

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Other Objects (12)

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Intracranial vasculopathy: an important organ damage in young adult patients with late-onset Pompe disease

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Alglucosidase alfa: 5 years of experience in late-onset Pompe disease

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Walking delay as leading symptom in late-onset Pompe disease

Intracranial vasculopathy: an important organ damage in young adult patients with late-onset Pompe disease

Late-Onset Pompe Disease Presenting with Isolated Tongue Involvement

Bright tongue sign in patients with late-onset Pompe disease

Alglucosidase alfa: 5 years of experience in late-onset Pompe disease

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Late-onset Pompe disease (LOPD) in Belgium: clinical characteristics and outcome measures

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Late-Onset Pompe Disease Presenting with Isolated Tongue Involvement

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Analysis of voice quality in patients with late-onset Pompe disease

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