STIG study: real-world data of long-term outcomes of adults with Pompe disease under enzyme replacement therapy with alglucosidase alfa
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1432-1459
- Extent
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Online-Ressource
- Language
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Englisch
- Notes
-
online resource.
- Bibliographic citation
-
STIG study: real-world data of long-term outcomes of adults with Pompe disease under enzyme replacement therapy with alglucosidase alfa ; day:5 ; month:2 ; year:2021 ; pages:1-11
Journal of neurology ; (5.2.2021), 1-11
- Creator
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Gutschmidt, Kristina
Musumeci, Olimpia
Díaz-Manera, Jordi
Chien, Yin-Hsiu
Knop, Karl Christian
Wenninger, Stephan
Montagnese, Federica
Pugliese, Alessia
Tavilla, Graziana
Alonso-Pérez, Jorge
Hwu, Paul Wuh-Liang
Toscano, Antonio
Schoser, Benedikt
- Contributor
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SpringerLink (Online service)
- DOI
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10.1007/s00415-021-10409-9
- URN
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urn:nbn:de:101:1-2021032817531852486377
- Rights
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
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14.08.2025, 11:02 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Gutschmidt, Kristina
- Musumeci, Olimpia
- Díaz-Manera, Jordi
- Chien, Yin-Hsiu
- Knop, Karl Christian
- Wenninger, Stephan
- Montagnese, Federica
- Pugliese, Alessia
- Tavilla, Graziana
- Alonso-Pérez, Jorge
- Hwu, Paul Wuh-Liang
- Toscano, Antonio
- Schoser, Benedikt
- SpringerLink (Online service)
Other Objects (12)
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Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in adult patients with Pompe disease
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Enzyme replacement therapy and fatigue in adults with Pompe disease
Long-Term Experience with Anaphylaxis and Desensitization to Alglucosidase Alfa in Pompe Disease
Impact of enzyme replacement therapy on survival in adults with Pompe disease
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Higher dose alglucosidase alfa is associated with improved overall survival in infantile-onset Pompe disease (IOPD): data from the Pompe Registry
Marsk Stig.
Flodmark, Stig
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Lundqvist, Stig
Improved Enzyme Replacement Therapy with Cipaglucosidase Alfa/Miglustat in Infantile Pompe Disease
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in adult patients with Pompe disease
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease
Enzyme replacement therapy and fatigue in adults with Pompe disease
Long-Term Experience with Anaphylaxis and Desensitization to Alglucosidase Alfa in Pompe Disease
Impact of enzyme replacement therapy on survival in adults with Pompe disease
Enzyme replacement therapy (ERT) in pompe disease
Higher dose alglucosidase alfa is associated with improved overall survival in infantile-onset Pompe disease (IOPD): data from the Pompe Registry
Marsk Stig.
Flodmark, Stig
Haglund, Stig
Lundqvist, Stig
Improved Enzyme Replacement Therapy with Cipaglucosidase Alfa/Miglustat in Infantile Pompe Disease
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in adult patients with Pompe disease
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease
Enzyme replacement therapy and fatigue in adults with Pompe disease
Long-Term Experience with Anaphylaxis and Desensitization to Alglucosidase Alfa in Pompe Disease
Impact of enzyme replacement therapy on survival in adults with Pompe disease
Enzyme replacement therapy (ERT) in pompe disease
Higher dose alglucosidase alfa is associated with improved overall survival in infantile-onset Pompe disease (IOPD): data from the Pompe Registry
Marsk Stig.
Flodmark, Stig
Haglund, Stig