Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1750-1172
- Extent
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Online-Ressource
- Language
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Englisch
- Notes
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online resource.
- Bibliographic citation
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Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies ; volume:7 ; number:1 ; day:24 ; month:11 ; year:2012 ; pages:1-11 ; date:12.2012
Orphanet journal of rare diseases ; 7, Heft 1 (24.11.2012), 1-11, 12.2012
- Creator
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Germain, Dominique P.
- Contributor
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Giugliani, Roberto
Hughes, Derralynn A.
Mehta, Atul
Nicholls, Kathy
Barisoni, Laura
Jennette, Charles J.
Bragat, Alexander
Castelli, Jeff
Sitaraman, Sheela
Lockhart, David J.
Boudes, Pol F.
SpringerLink (Online service)
- DOI
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10.1186/1750-1172-7-91
- URN
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urn:nbn:de:1111-2016050120465
- Rights
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Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
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14.08.2025, 10:44 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Germain, Dominique P.
- Giugliani, Roberto
- Hughes, Derralynn A.
- Mehta, Atul
- Nicholls, Kathy
- Barisoni, Laura
- Jennette, Charles J.
- Bragat, Alexander
- Castelli, Jeff
- Sitaraman, Sheela
- Lockhart, David J.
- Boudes, Pol F.
- SpringerLink (Online service)
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