Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study
- Standort
-
Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
-
2193-6536
- Umfang
-
Online-Ressource
- Sprache
-
Englisch
- Anmerkungen
-
online resource.
- Erschienen in
-
Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study ; day:21 ; month:10 ; year:2022 ; pages:1-17
Neurology and Therapy ; (21.10.2022), 1-17
- Urheber
-
Vázquez-Costa, Juan F.
Branas-Pampillón, María
Medina-Cantillo, Julita
Povedano, Mónica
Pitarch-Castellano, Inmaculada
López-Lobato, Mercedes
Fernández-Ramos, Joaquín A.
Lafuente-Hidalgo, Miguel
Rojas-García, Ricard
Caballero-Caballero, José M.
Málaga, Ignacio
Eirís-Puñal, Jesús
Lemus, Mencía De
Cattinari, María G.
Cabello-Moruno, Rosana
Díaz-Abós, Paola
Sánchez-Menéndez, Victoria
Rebollo, Pablo
Maurino, Jorge
Madruga-Garrido, Marcos
- Beteiligte Personen und Organisationen
-
SpringerLink (Online service)
- DOI
-
10.1007/s40120-022-00411-2
- URN
-
urn:nbn:de:101:1-2023010708595546493836
- Rechteinformation
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
15.08.2025, 07:35 MESZ
Datenpartner
Dieses Objekt wird bereitgestellt von:
Deutsche Nationalbibliothek. Bei Fragen zum Objekt wenden Sie sich bitte an den Datenpartner.
Deutsche Nationalbibliothek. Bei Fragen zum Objekt wenden Sie sich bitte an den Datenpartner.
Beteiligte
- Vázquez-Costa, Juan F.
- Branas-Pampillón, María
- Medina-Cantillo, Julita
- Povedano, Mónica
- Pitarch-Castellano, Inmaculada
- López-Lobato, Mercedes
- Fernández-Ramos, Joaquín A.
- Lafuente-Hidalgo, Miguel
- Rojas-García, Ricard
- Caballero-Caballero, José M.
- Málaga, Ignacio
- Eirís-Puñal, Jesús
- Lemus, Mencía De
- Cattinari, María G.
- Cabello-Moruno, Rosana
- Díaz-Abós, Paola
- Sánchez-Menéndez, Victoria
- Rebollo, Pablo
- Maurino, Jorge
- Madruga-Garrido, Marcos
- SpringerLink (Online service)
Ähnliche Objekte (12)
Molecular mechanisms of cytoskeletal dysregulations in Spinal Muscular Atrophy (SMA)
Development of antisense oligonucleotide combinatorial therapies for spinal muscular atrophy (SMA)
Cytoskeletal dysregulation in the motoneuron disease Spinal Muscular Atrophy (SMA)
Letter to the Editor Regarding “Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study”
Spinal muscular atrophy
Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study)
Dynamics and regulation of the actin cytoskeleton in the motoneuron disease Spinal Muscular Atrophy (SMA)
Observation of the natural course of type 3 spinal muscular atrophy: data from the polish registry of spinal muscular atrophy
Systematic Literature Review to Assess Economic Evaluations in Spinal Muscular Atrophy (SMA)
Identification and characterization of spinal muscular atrophy (SMA) modifiers - insight from cellular and vertebrate disease models
network-biology based approach for the evaluation of novel treatment targets for Spinal Muscular Atrophy (SMA)
Disease burden of spinal muscular atrophy in Germany
Molecular mechanisms of cytoskeletal dysregulations in Spinal Muscular Atrophy (SMA)
Development of antisense oligonucleotide combinatorial therapies for spinal muscular atrophy (SMA)
Cytoskeletal dysregulation in the motoneuron disease Spinal Muscular Atrophy (SMA)
Letter to the Editor Regarding “Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study”
Spinal muscular atrophy
Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study)
Dynamics and regulation of the actin cytoskeleton in the motoneuron disease Spinal Muscular Atrophy (SMA)
Observation of the natural course of type 3 spinal muscular atrophy: data from the polish registry of spinal muscular atrophy
Systematic Literature Review to Assess Economic Evaluations in Spinal Muscular Atrophy (SMA)
Identification and characterization of spinal muscular atrophy (SMA) modifiers - insight from cellular and vertebrate disease models
network-biology based approach for the evaluation of novel treatment targets for Spinal Muscular Atrophy (SMA)
Disease burden of spinal muscular atrophy in Germany
Molecular mechanisms of cytoskeletal dysregulations in Spinal Muscular Atrophy (SMA)
Development of antisense oligonucleotide combinatorial therapies for spinal muscular atrophy (SMA)
Cytoskeletal dysregulation in the motoneuron disease Spinal Muscular Atrophy (SMA)
Letter to the Editor Regarding “Validation of a Set of Instruments to Assess Patient- and Caregiver-Oriented Measurements in Spinal Muscular Atrophy: Results of the SMA-TOOL Study”
Spinal muscular atrophy
Design of a Non-Interventional Study to Validate a Set of Patient- and Caregiver-Oriented Measurements to Assess Health Outcomes in Spinal Muscular Atrophy (SMA-TOOL Study)
Dynamics and regulation of the actin cytoskeleton in the motoneuron disease Spinal Muscular Atrophy (SMA)
Observation of the natural course of type 3 spinal muscular atrophy: data from the polish registry of spinal muscular atrophy
Systematic Literature Review to Assess Economic Evaluations in Spinal Muscular Atrophy (SMA)
Identification and characterization of spinal muscular atrophy (SMA) modifiers - insight from cellular and vertebrate disease models
network-biology based approach for the evaluation of novel treatment targets for Spinal Muscular Atrophy (SMA)