Clinical efficacy of the enzyme replacement therapy in patients with late-onset Pompe disease: a systematic review and a meta-analysis

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Location: Deutsche Nationalbibliothek Frankfurt am Main

ISSN: 1432-1459

Extent: Online-Ressource

Language: Englisch

Notes: online resource.

Bibliographic citation: Clinical efficacy of the enzyme replacement therapy in patients with late-onset Pompe disease: a systematic review and a meta-analysis ; day:13 ; month:4 ; year:2021 ; pages:1-9
Journal of neurology ; (13.4.2021), 1-9

Creator: Sarah, Berli
Giovanna, Brandi
Emanuela, Keller
Nadi, Najia
Josè, Vitale
Alberto, Pagnamenta

Contributor: SpringerLink (Online service)

DOI: 10.1007/s00415-021-10526-5

URN: urn:nbn:de:101:1-2021060221585873078486

Rights: Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.

Last update: 14.08.2025, 10:54 AM CEST

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Sarah, Berli
Giovanna, Brandi
Emanuela, Keller
Nadi, Najia
Josè, Vitale
Alberto, Pagnamenta
SpringerLink (Online service)

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Clinical efficacy of the enzyme replacement therapy in patients with late-onset Pompe disease: a systematic review and a meta-analysis

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Other Objects (12)

The impact of interrupting enzyme replacement therapy in late-onset Pompe disease

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Hearing characteristics of infantile-onset Pompe disease after early enzyme-replacement therapy

Bright tongue sign in patients with late-onset Pompe disease

Walking delay as leading symptom in late-onset Pompe disease

Enzyme replacement therapy (ERT) in pompe disease

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Fatigue: an important feature of late-onset Pompe disease

Late-Onset Pompe Disease Presenting with Isolated Tongue Involvement

Hearing characteristics of infantile-onset Pompe disease after early enzyme-replacement therapy

Bright tongue sign in patients with late-onset Pompe disease

Walking delay as leading symptom in late-onset Pompe disease

Enzyme replacement therapy (ERT) in pompe disease

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Fatigue: an important feature of late-onset Pompe disease

Late-Onset Pompe Disease Presenting with Isolated Tongue Involvement

Hearing characteristics of infantile-onset Pompe disease after early enzyme-replacement therapy

Bright tongue sign in patients with late-onset Pompe disease

Walking delay as leading symptom in late-onset Pompe disease

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