CRISPR-mediated generation and characterization of a Gaa homozygous c.1935C>A (p.D645E) Pompe disease knock-in mouse model recapitulating human infantile onset-Pompe disease
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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2045-2322
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
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online resource.
- Erschienen in
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CRISPR-mediated generation and characterization of a Gaa homozygous c.1935C>A (p.D645E) Pompe disease knock-in mouse model recapitulating human infantile onset-Pompe disease ; volume:12 ; number:1 ; day:14 ; month:12 ; year:2022 ; pages:1-13 ; date:12.2022
Scientific reports ; 12, Heft 1 (14.12.2022), 1-13, 12.2022
- Urheber
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Kan, Shih-hsin
Huang, Jeffrey Y.
Harb, Jerry
Rha, Allisandra
Dalton, Nancy D.
Christensen, Chloe
Chan, Yunghang
Davis-Turak, Jeremy
Neumann, Jonathan
Wang, Raymond Y.
- Beteiligte Personen und Organisationen
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SpringerLink (Online service)
- DOI
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10.1038/s41598-022-25914-8
- URN
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urn:nbn:de:101:1-2023022321013407620471
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
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14.08.2025, 11:00 MESZ
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Beteiligte
- Kan, Shih-hsin
- Huang, Jeffrey Y.
- Harb, Jerry
- Rha, Allisandra
- Dalton, Nancy D.
- Christensen, Chloe
- Chan, Yunghang
- Davis-Turak, Jeremy
- Neumann, Jonathan
- Wang, Raymond Y.
- SpringerLink (Online service)
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