- Location
-
Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
-
1179-1896
- Extent
-
Online-Ressource
- Language
-
Englisch
- Notes
-
online resource.
- Bibliographic citation
-
Costs of Illness of Spinal Muscular Atrophy: A Systematic Review ; day:12 ; month:2 ; year:2021 ; pages:1-20
Applied health economics and health policy ; (12.2.2021), 1-20
- Creator
- Contributor
-
SpringerLink (Online service)
- DOI
-
10.1007/s40258-020-00624-2
- URN
-
urn:nbn:de:101:1-2021040308015675079247
- Rights
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
-
14.08.2025, 10:45 AM CEST
Data provider
This object is provided by:
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Landfeldt, Erik
- Pechmann, Astrid
- McMillan, Hugh J.
- Lochmüller, Hanns
- Sejersen, Thomas
- SpringerLink (Online service)
Other Objects (12)
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Costs of illness of spinal muscular atrophy: a systematic review
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Incomplete description of the current body of evidence of the health economics of Duchenne muscular dystrophy
The TREAT‐NMD DMD global database: analysis of more than 7,000 duchenne muscular dystrophy mutations
Clinical outcomes in Duchenne Muscular Dystrophy: a study of 5345 patients from the TREAT-NMD DMD global database
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Prevalence, incidence and carrier frequency of 5q–linked spinal muscular atrophy – a literature review
Tumor necrosis factor receptor SF10A (TNFRSF10A) SNPs correlate with corticosteroid response in duchenne muscular dystrophy
Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Correction to: Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Cathepsin D as biomarker in CSF of nusinersen‐treated patients with spinal muscular atrophy
Economic Evaluation in Duchenne Muscular Dystrophy: Model Frameworks for Cost-Effectiveness Analysis
Costs of illness of spinal muscular atrophy: a systematic review
Transition from childhood to adulthood in Duchenne muscular dystrophy (DMD)
Incomplete description of the current body of evidence of the health economics of Duchenne muscular dystrophy
The TREAT‐NMD DMD global database: analysis of more than 7,000 duchenne muscular dystrophy mutations
Clinical outcomes in Duchenne Muscular Dystrophy: a study of 5345 patients from the TREAT-NMD DMD global database
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Prevalence, incidence and carrier frequency of 5q–linked spinal muscular atrophy – a literature review
Tumor necrosis factor receptor SF10A (TNFRSF10A) SNPs correlate with corticosteroid response in duchenne muscular dystrophy
Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Correction to: Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Cathepsin D as biomarker in CSF of nusinersen‐treated patients with spinal muscular atrophy