A phase 3 randomized study evaluating sialic acid extended-release for GNE myopathy
- Standort
-
Deutsche Nationalbibliothek Frankfurt am Main
- Umfang
-
Online-Ressource
- Sprache
-
Englisch
- Anmerkungen
-
Neurology. - 92, 18 (2019) , E2109-E2117, ISSN: 1526-632X
- Ereignis
-
Veröffentlichung
- (wo)
-
Freiburg
- (wer)
-
Universität
- (wann)
-
2019
- Urheber
-
Lochmüller, Hanns
Behin, Anthony
Caraco, Yoseph
Lau, Heather
Mirabella, Massimiliano
Tournev, Ivailo
Tarnopolsky, Mark
Pogoryelova, Oksana
Woods, Catherine
Lai, Alexander
Shah, Jinay
Koutsoukos, Tony
Skrinar, Alison
Mansbach, Hank
Kakkis, Emil
Mozaffar, Tahseen
- DOI
-
10.1212/WNL.0000000000006932
- URN
-
urn:nbn:de:bsz:25-freidok-1508380
- Rechteinformation
-
Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
15.08.2025, 07:38 MESZ
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Beteiligte
- Lochmüller, Hanns
- Behin, Anthony
- Caraco, Yoseph
- Lau, Heather
- Mirabella, Massimiliano
- Tournev, Ivailo
- Tarnopolsky, Mark
- Pogoryelova, Oksana
- Woods, Catherine
- Lai, Alexander
- Shah, Jinay
- Koutsoukos, Tony
- Skrinar, Alison
- Mansbach, Hank
- Kakkis, Emil
- Mozaffar, Tahseen
- Universität
Entstanden
- 2019
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