Works:
- Risdiplam improves subjective swallowing quality in non-ambulatory adult patients with 5q-spinal muscular atrophy despite advanced motor impairment
- Effectiveness of Nusinersen in Adolescents and Adults with Spinal Muscular Atrophy: Systematic Review and Meta-analysis
- Iatrogenic botulism after intragastric botulinum neurotoxin injections - a major outbreak
- Astrozyten-vermittelte Glutamat-Toxizität bei der Spinalen Muskelatrophie