STIG study: real-world data of long-term outcomes of adults with Pompe disease under enzyme replacement therapy with alglucosidase alfa
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1432-1459
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
-
online resource.
- Erschienen in
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STIG study: real-world data of long-term outcomes of adults with Pompe disease under enzyme replacement therapy with alglucosidase alfa ; day:5 ; month:2 ; year:2021 ; pages:1-11
Journal of neurology ; (5.2.2021), 1-11
- Urheber
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Gutschmidt, Kristina
Musumeci, Olimpia
Díaz-Manera, Jordi
Chien, Yin-Hsiu
Knop, Karl Christian
Wenninger, Stephan
Montagnese, Federica
Pugliese, Alessia
Tavilla, Graziana
Alonso-Pérez, Jorge
Hwu, Paul Wuh-Liang
Toscano, Antonio
Schoser, Benedikt
- Beteiligte Personen und Organisationen
-
SpringerLink (Online service)
- DOI
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10.1007/s00415-021-10409-9
- URN
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urn:nbn:de:101:1-2021032817531852486377
- Rechteinformation
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
14.08.2025, 11:02 MESZ
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Beteiligte
- Gutschmidt, Kristina
- Musumeci, Olimpia
- Díaz-Manera, Jordi
- Chien, Yin-Hsiu
- Knop, Karl Christian
- Wenninger, Stephan
- Montagnese, Federica
- Pugliese, Alessia
- Tavilla, Graziana
- Alonso-Pérez, Jorge
- Hwu, Paul Wuh-Liang
- Toscano, Antonio
- Schoser, Benedikt
- SpringerLink (Online service)
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