Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

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Location: Deutsche Nationalbibliothek Frankfurt am Main

ISSN: 1750-1172

Extent: Online-Ressource

Language: Englisch

Notes: online resource.

Bibliographic citation: Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR ; volume:13 ; number:1 ; day:1 ; month:2 ; year:2018 ; pages:1-9 ; date:12.2018
Orphanet journal of rare diseases ; 13, Heft 1 (1.2.2018), 1-9, 12.2018

Keyword: Biopharmazie
Pharmakodynamik
Pharmakokinetik

Creator: Richter, Trevor

Contributor: Janoudi, Ghayath
Amegatse, William
Nester-Parr, Sandra
SpringerLink (Online service)

DOI: 10.1186/s13023-018-0762-1

URN: urn:nbn:de:1111-2018032024025

Rights: Der Zugriff auf das Objekt ist unbeschränkt möglich.

Last update: 14.08.2025, 10:47 AM CEST

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Richter, Trevor
Janoudi, Ghayath
Amegatse, William
Nester-Parr, Sandra
SpringerLink (Online service)

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Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

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