Real-World Experience of Carglumic Acid for Methylmalonic and Propionic Acidurias: An Interim Analysis of the Multicentre Observational PROTECT Study
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- Extent
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1 Online-Ressource.
- Language
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Englisch
- Bibliographic citation
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Real-World Experience of Carglumic Acid for Methylmalonic and Propionic Acidurias: An Interim Analysis of the Multicentre Observational PROTECT Study ; day:10 ; month:1 ; year:2024 ; pages:1-12
Drugs in R & D ; (10.1.2024), 1-12
- Creator
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Yap, Sufin
Lamireau, Delphine
Feillet, Francois
Ruiz Gomez, Angeles
Davison, James
Tangeraas, Trine
Giordano, Vincenzo
- Contributor
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SpringerLink (Online service)
- DOI
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10.1007/s40268-023-00449-z
- URN
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urn:nbn:de:101:1-2024032509410276283930
- Rights
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
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14.08.2025, 10:59 AM CEST
Data provider
This object is provided by:
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Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Yap, Sufin
- Lamireau, Delphine
- Feillet, Francois
- Ruiz Gomez, Angeles
- Davison, James
- Tangeraas, Trine
- Giordano, Vincenzo
- SpringerLink (Online service)
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Catalytic ketonization of propionic acid. Green chemistry in practice
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Biomarkers for drug development in propionic and methylmalonic acidemias
Interim analyses of a first-in-human phase 1/2 mRNA trial for propionic acidaemia
Evaluation of source data verification in a multicentre cancer trial (PROTECT)
Prevalence of propionic acidemia in China
Publisher Correction: Interim analyses of a first-in-human phase 1/2 mRNA trial for propionic acidaemia
Improved production of propionic acid using genome shuffling
Antenatal nephromegaly and propionic acidemia: a case report
Primary breast double-hit lymphoma management and outcomes: a real-world multicentre experience
Propionic acid production through anaerobic fermentation of food waste
Propionic acidaemia crisis: a specific DWI finding—case report
Catalytic ketonization of propionic acid. Green chemistry in practice
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