Impact of enzyme replacement therapy on survival in adults with Pompe disease: results from a prospective international observational study
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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1750-1172
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
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online resource.
- Erschienen in
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Impact of enzyme replacement therapy on survival in adults with Pompe disease: results from a prospective international observational study ; volume:8 ; number:1 ; day:27 ; month:3 ; year:2013 ; pages:1-7 ; date:12.2013
Orphanet journal of rare diseases ; 8, Heft 1 (27.3.2013), 1-7, 12.2013
- Urheber
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Güngör, Deniz
- Beteiligte Personen und Organisationen
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Kruijshaar, Michelle E.
Plug, Iris
D’Agostino, Ralph B.
Hagemans, Marloes LC
van Doorn, Pieter A.
Reuser, Arnold JJ
van der Ploeg, Ans T.
SpringerLink (Online service)
- DOI
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10.1186/1750-1172-8-49
- URN
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urn:nbn:de:1111-2016050122487
- Rechteinformation
-
Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
-
14.08.2025, 10:52 MESZ
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Beteiligte
- Güngör, Deniz
- Kruijshaar, Michelle E.
- Plug, Iris
- D’Agostino, Ralph B.
- Hagemans, Marloes LC
- van Doorn, Pieter A.
- Reuser, Arnold JJ
- van der Ploeg, Ans T.
- SpringerLink (Online service)
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