Splice-Modulating Antisense Oligonucleotides as Therapeutics for Inherited Metabolic Diseases
- Location
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Deutsche Nationalbibliothek Frankfurt am Main
- Extent
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1 Online-Ressource.
- Language
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Englisch
- Bibliographic citation
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Splice-Modulating Antisense Oligonucleotides as Therapeutics for Inherited Metabolic Diseases ; volume:38 ; number:2 ; day:22 ; month:1 ; year:2024 ; pages:177-203 ; date:3.2024
BioDrugs ; 38, Heft 2 (22.1.2024), 177-203, 3.2024
- Creator
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Chen, Suxiang
Heendeniya, Saumya Nishanga
Le, Bao T.
Rahimizadeh, Kamal
Rabiee, Navid
Zahra, Qurat ul ain
Veedu, Rakesh N.
- Contributor
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SpringerLink (Online service)
- DOI
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10.1007/s40259-024-00644-7
- URN
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urn:nbn:de:101:1-2405101047155.763634380888
- Rights
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Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Last update
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14.08.2025, 10:58 AM CEST
Data provider
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Deutsche Nationalbibliothek. If you have any questions about the object, please contact the data provider.
Associated
- Chen, Suxiang
- Heendeniya, Saumya Nishanga
- Le, Bao T.
- Rahimizadeh, Kamal
- Rabiee, Navid
- Zahra, Qurat ul ain
- Veedu, Rakesh N.
- SpringerLink (Online service)
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Antisense oligonucleotides: recent progress in the treatment of various diseases
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Intracellular Delivery of Antisense Oligonucleotides by Tri‐Branched Cyclic Disulfide Units
Engineering Antisense Oligonucleotides for Site-directed RNA Editing with Endogenous ADAR
Functionalized halloysite nanotube-based carrier for intracellular delivery of antisense oligonucleotides
Mismatched single stranded antisense oligonucleotides can induce efficient dystrophin splice switching
Tritium labeling of antisense oligonucleotides via different conjugation agents
Nonviral delivery systems for antisense oligonucleotide therapeutics
Challenges to oligonucleotides-based therapeutics for Duchenne muscular dystrophy
Gephyrin antisense oligonucleotides prevent glycine receptor clustering in spinal neurons
Minimal structural modifications of antisense oligonucleotides conveying stability towards endonucleases
Respirable antisense oligonucleotides: a new drug class for respiratory disease
Antisense oligonucleotides: recent progress in the treatment of various diseases
Splicing modulation via antisense oligonucleotides in recessive dystrophic epidermolysis bullosa
Intracellular Delivery of Antisense Oligonucleotides by Tri‐Branched Cyclic Disulfide Units
Engineering Antisense Oligonucleotides for Site-directed RNA Editing with Endogenous ADAR