CRISPR/Cas9-mediated excision of ALS/FTD-causing hexanucleotide repeat expansion in C9ORF72 rescues major disease mechanisms in vivo and in vitro
- Standort
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Deutsche Nationalbibliothek Frankfurt am Main
- ISSN
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2041-1723
- Umfang
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Online-Ressource
- Sprache
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Englisch
- Anmerkungen
-
online resource.
- Erschienen in
-
CRISPR/Cas9-mediated excision of ALS/FTD-causing hexanucleotide repeat expansion in C9ORF72 rescues major disease mechanisms in vivo and in vitro ; volume:13 ; number:1 ; day:21 ; month:10 ; year:2022 ; pages:1-17 ; date:12.2022
Nature Communications ; 13, Heft 1 (21.10.2022), 1-17, 12.2022
- Urheber
-
Meijboom, Katharina E.
Abdallah, Abbas
Fordham, Nicholas P.
Nagase, Hiroko
Rodriguez, Tomás
Kraus, Carolyn
Gendron, Tania F.
Krishnan, Gopinath
Esanov, Rustam
Andrade, Nadja S.
Rybin, Matthew J.
Ramic, Melina
Stephens, Zachary D.
Edraki, Alireza
Blackwood, Meghan T.
Kahriman, Aydan
Henninger, Nils
Kocher, Jean-Pierre A.
Benatar, Michael
Brodsky, Michael H.
Petrucelli, Leonard
Gao, Fen-Biao
Sontheimer, Erik J.
Brown, Robert H.
Zeier, Zane
Müller, Christian L.
- Beteiligte Personen und Organisationen
-
SpringerLink (Online service)
- DOI
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10.1038/s41467-022-33332-7
- URN
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urn:nbn:de:101:1-2023010709215706058794
- Rechteinformation
-
Open Access; Der Zugriff auf das Objekt ist unbeschränkt möglich.
- Letzte Aktualisierung
- 15.08.2025, 05:20 UTC
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Beteiligte
- Meijboom, Katharina E.
- Abdallah, Abbas
- Fordham, Nicholas P.
- Nagase, Hiroko
- Rodriguez, Tomás
- Kraus, Carolyn
- Gendron, Tania F.
- Krishnan, Gopinath
- Esanov, Rustam
- Andrade, Nadja S.
- Rybin, Matthew J.
- Ramic, Melina
- Stephens, Zachary D.
- Edraki, Alireza
- Blackwood, Meghan T.
- Kahriman, Aydan
- Henninger, Nils
- Kocher, Jean-Pierre A.
- Benatar, Michael
- Brodsky, Michael H.
- Petrucelli, Leonard
- Gao, Fen-Biao
- Sontheimer, Erik J.
- Brown, Robert H.
- Zeier, Zane
- Müller, Christian L.
- SpringerLink (Online service)
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